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Hemophilia B, Severe

Showing 1 - 25 of >10,000

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Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)

Not yet recruiting
  • Hemophilia B Without Inhibitor
  • Low dose KL001
  • +2 more
  • (no location specified)
Nov 5, 2023

Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)

Not yet recruiting
  • Hemophilia B Without Inhibitor
  • Low dose KL001
  • +2 more
  • (no location specified)
Nov 5, 2023

Hemophilia A, Hemophilia B Trial (SerpinPC)

Not yet recruiting
  • Hemophilia A
  • Hemophilia B
  • (no location specified)
Mar 16, 2023

Hemophilia B Trial (CSL222 (AAV5-hFIXco-Padua))

Not yet recruiting
  • Hemophilia B
  • CSL222 (AAV5-hFIXco-Padua)
  • (no location specified)
Aug 14, 2023

Hemophilia B Trial in Beijing (Sodium valproate extended-release tablets)

Recruiting
  • Hemophilia B
  • Sodium valproate extended-release tablets
  • Beijing, China
    PLA General Hospital
Jun 17, 2023

Hemophilia A, Hemophilia B Trial in Korea, Republic of, South Africa, Taiwan (marstacimab)

Recruiting
  • Hemophilia A
  • Hemophilia B
  • Seoul, Seoul-teukbyeolsi [seoul], Korea, Republic of
  • +3 more
Jan 18, 2023

Severe Hemophilia Non-Interventional Study

Not yet recruiting
  • Hemophilia A
  • Hemophilia B
  • No Intervention
  • Rzeszów, Podkarpackie, Poland
  • +2 more
Dec 8, 2022

Hemophilia B Trial in Denmark, Germany, Netherlands (AAV5-hFIX)

Completed
  • Hemophilia B
  • AAV5-hFIX
  • Copenhagen, Denmark
  • +6 more
Jun 1, 2022

Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B

Active, not recruiting
  • Hemophilia B
  • AAV5-hFIX
  • Berlin, Germany
  • +5 more
Jan 17, 2023

Reliability and Validity of the Turkish Version of the PedHAL

Not yet recruiting
  • Hemophilia
  • +2 more
    • Gaziantep, Şahinbey, Turkey
      Hasan Kalyoncu University
    Jun 2, 2023

    In Vitro Correction of Thrombin Generation by Concizumab for

    Recruiting
    • Hemophilia
    • thrombin generation measurement
    • Saint-Etienne, France
      CHU Saint-Etienne
    Dec 13, 2022

    Hemophilia Trial in Orange (Fitusiran, Clotting factor concentrates (CFC) or bypassing agents (BPA), Antithrombin concentrate

    Recruiting
    • Hemophilia
    • Orange, California
      Center for Inherited Blood Disorders (CIBD)-Site Number:8400012
    Feb 2, 2023

    Hemophilia B Trial in India (Nonacog alfa)

    Completed
    • Hemophilia B
    • Nonacog alfa
    • Surat, Gujarat, India
    • +4 more
    Jun 29, 2022

    Hemophilia Trial in Yongin-si (MG1113)

    Not yet recruiting
    • Hemophilia
    • MG1113
    • Yongin-si, Gyeonggi-do, Korea, Republic of
      GC Biopharma Corp.
    Aug 9, 2022

    Hemophilia Trial in Tianjin (KN057 dose?, KN057 dose ?, KN057 dose ?)

    Recruiting
    • Hemophilia
    • KN057 doseⅠ
    • +2 more
    • Tianjin, Tianjin, China
    • +1 more
    Jul 20, 2022

    Hemophilia A, Hemophilia B Trial in Worldwide (Fitusiran (SAR439774))

    Active, not recruiting
    • Hemophilia A
    • Hemophilia B
    • Fitusiran (SAR439774)
    • Ann Arbor, Michigan
    • +11 more
    Aug 4, 2022

    Hemophilia B Trial in Washington (SB-FIX)

    Terminated
    • Hemophilia B
    • SB-FIX
    • Washington, District of Columbia
      Georgetown University Medical Center
    Mar 8, 2022

    DTX101 (AAVrh10FIX) in Moderate/Severe to Severe Hemophilia B

    Completed
    • Hemophilia B
      • Little Rock, Arkansas
      • +4 more
      Jan 4, 2022

      Hemophilia A, Hemophilia B Trial in Tbilisi, Chisinau, Merthyr Tydfil (SerpinPC, Placebo)

      Active, not recruiting
      • Hemophilia A
      • Hemophilia B
      • Tbilisi, Georgia
      • +2 more
      Jun 23, 2022

      Liver Biopsy In Haemophilia Gene Therapy

      Not yet recruiting
      • Hemophilia B, Severe
      • Hemophilia A, Severe
        • (no location specified)
        Mar 23, 2021

        Hemophilia B Trial in Worldwide (AAV5-hFIXco-Padua)

        Active, not recruiting
        • Hemophilia B
        • AAV5-hFIXco-Padua
        • Factor IX (FIX)
        • Phoenix, Arizona
        • +32 more
        Sep 26, 2022

        Severe Hemophilia A, Moderate Hemophilia A Trial in Worldwide (Emicizumab)

        Recruiting
        • Severe Hemophilia A
        • Moderate Hemophilia A
        • Los Angeles, California
        • +10 more
        Aug 12, 2022

        Hemophilia B Trial in United States (AAV5-hFIXco-Padua (AMT-061))

        Active, not recruiting
        • Hemophilia B
        • AAV5-hFIXco-Padua (AMT-061)
        • Los Angeles, California
        • +3 more
        May 17, 2022

        Hemophilia A, Hemophilia B Trial in Worldwide (PF-06741086)

        Recruiting
        • Hemophilia A
        • Hemophilia B
        • Tampa, Florida
        • +62 more
        Dec 14, 2022

        Hemophilia A, Hemophilia B Trial in Worldwide (PF-06741086)

        Recruiting
        • Hemophilia A
        • Hemophilia B
        • Hong Kong, Hong Kong
        • +17 more
        Jul 21, 2022